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BioMarin Presents New Phase 3, Four-Year Data Underscoring Long-Term Safety and Efficacy of ROCTAVIAN® (valoctocogene roxaparvovec-rvox) at International Society on Thrombosis and Haemosta...

BioMarin Pharmaceutical Inc.  (BMRN) 
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PDF Additional Data Show Meaningful Impact of ROCTAVIAN on Health-Related Quality of Life (HRQoL) SAN RAFAEL, Calif. June 7, 2024 /PRNewswire/ -- BioMarin Pharmaceutical [Read more]